
- A UPMC doctor waited years for a needed drug to get approval. The FDA finally gave it Pittsburgh Post-Gazette
- FDA greenlights Stealth Bio’s injection as 1st treatment for Barth syndrome Fierce Pharma
- FDA gives approval for treatment of rare disease affecting Hall Co. family AccessWdun
- US FDA approves first treatment for rare, life-threatening disease in males Reuters
- Stealth Wins Expedited FDA Nod for First-Ever Barth Syndrome Treatment BioSpace
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